Every Day We Change Lives People living with rare and devastating diseases are our Guiding Star. We believe it is our responsibility to listen to, understand, and change the lives of patients and those who work tirelessly to help them. Our mission is to transform the lives of people affected by rare diseases and devastating conditions by continuously innovating and creating meaningful value in all that we do. In doing so, we change lives for the better- ours, people living with rare diseases, and the communities we serve. Every day.